Gamze BORA, Ayşe YEŞBEK-KAYMAZ, Can Ebru BEKİRCAN-KURT, Vildan Göknur HALİLOĞLU, Haluk Aydin TOPALOĞLU, Hayat ERDEM-YURTER, Sevim ERDEM-ÖZDAMAR
Turkish Journal of Medical Sciences
203-211
Spinal muscular atrophy, therapeutic approaches, clinical trials